Tag Archive: Raymond G. Perelman Center for Cellular and Molecular Therapeutics

Dec 21 2017

Groundbreaking Gene Therapy Approved for Inherited Retinal Blindness

More than a decade of studies led by researchers at Children’s Hospital of Philadelphia and the University of Pennsylvania culminated this week with the U.S. Food and Drug Administration’s approval of an innovative one-time gene therapy product indicated for the treatment of patients with a rare, inherited form of retinal blindness.

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Jul 29 2016

CHOP Research In the News: New Rare Disease, FA Woodstock, Bioengineering, and Protecting Toddlers from Child Abuse

CHOP Research In the NewsOne of the things that is so exciting about research at CHOP is that our researchers are working to improve the health and lives of children in such a broad range of ways.

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