Tag Archive: Mulchandani-Bhoj-Conlin Syndrome
Elizabeth Bhoj, MD, PhD, modestly admits she had a May that most physicians dream of. The clinician-researcher in the at the Children’s Hospital of Philadelphia capped off the month by earning three major distinctions: the William K. Bowes Jr. Award in Medical Genetics, the Burroughs Wellcome Fund’s Career Awards for Medical Scientists with a $700,000 prize, and the Society for Pediatric Research’s (SPR) Physician Scientist Award.
It was a big year for children’s health: We celebrated the U.S. Food and Drug Administration’s approval of the world’s first chimeric antigen receptor (CAR)-T cell therapy this September, followed closely by approval of the very first gene therapy to treat inherited blindness this month — both of which have their roots at Children’s Hospital of Philadelphia and the University of Pennsylvania. But besides the big headline-making breakthroughs (brilliant as they are), we wanted to know what other stories captivated our readers in 2017.
“Bold” is perhaps the best word to describe this week’s roundup of Research Institute news, as Children’s Hospital of Philadelphia nurses and investigators alike made headlines for their experimental work in pediatric CAR T-cell therapy.