Tag Archive: LINCL-Batten disease

Feb 9 2016

CHOP Research Annual Report 2015: The Future Is Here — Don’t Miss It

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Scientific minds are imagining. Sophisticated machines are harnessing genetic data. An invisible universe of microbes is revealing new insights into disease. Discoveries are changing children’s worlds. Every second of every day is filled with wonder at The Children’s Hospital of Philadelphia Research Institute.

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Nov 12 2015

Targeted Gene Therapy Aimed at Devastating Childhood Disease

active nerve cell illustrationWhen something important is missing, we often search for a replacement. After many years of looking, a team of researchers at The Children’s Hospital of Philadelphia and the University of Missouri have found a way to substitute for a missing gene linked to a relentless childhood neurodegenerative disease.

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