Tag Archive: clinical trial

Feb 9 2018

CAR-T Cell Therapy Benefits, Leukodystrophy Research, Social Innovation Awards, Teen Screen Time

We’re finishing off the week with a winning touchdown of news that gives us as much pride for our researchers as we have for our Philadelphia Eagles in Sunday’s Super Bowl. In this roundup of recent headlines, we cover new results from the game-changing immunotherapy for acute lymphoblastic leukemia (ALL) pioneered by Children’s Hospital of Philadelphia and University of Pennsylvania scientists, announce a generous family donation that will benefit research at our Leukodystrophy Center of Excellence, and share new awards and advances from our talented investigators and clinicians.

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Mar 30 2015

Watch CANCER: THE EMPEROR OF ALL MALADIES

CANCERThe history of our understanding and approach to cancer are at the center of CANCER: THE EMPEROR OF ALL MALADIES, a film directed by Barak Goodman and executive produced by Ken Burns.

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Oct 8 2014

Experts’ Research Leads to Rare Disease Clinical Trial

rare diseaseAs rare pediatric diseases go, Fibrodysplasia Ossificans Progressiva (FOP) is about as rare and debilitating as they come, affecting roughly one in two million people around the world.

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Nov 27 2013

Developing a Promising Approach to Treat Congenital Hyperinsulinism

Congenital Hyperinsulinism“It’s like the opposite of diabetes.” That is the simplest way to explain congenital hyperinsulinism (HI), a rare disease in which the pancreas makes too much of the hormone insulin, causing blood glucose to plummet.

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Dec 9 2012

Leukemia Patient Cancer-Free After Novel Treatment With Engineered Immune Cells

Emma relapses with acute lymphoblastic leukemia

Dr. Stephen Grupp's patient, Emma, relapses with acute lymphoblastic leukemia (ALL) in April 2011.

Cancer therapy for children has come a long way over the last several decades, and the cure rate for some forms of pediatric cancer is at an all-time high. Although this success rate offers tremendous hope and optimism, there are some children whose disease fails to respond to conventional treatment, leaving doctors to explore novel ways to conquer cancer.

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