Category Archive: Raymond G. Perelman Center for Cellular & Molecular Therapeutics

Mar 15 2018

Four Women in Science: What Inspires Them to Make Breakthroughs

In the halls and history of Children’s Hospital of Philadelphia and its Research Institute, you don’t have to search far to find role models who thrive in science fields that have been, historically, underrepresented by women.

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Sep 8 2017

CAR-T Cell Approval, Hope on Wheels, Task Force on Pregnant Women, Taking Flight for Autism, NFL Concussion Research, Doug Wallace

CHOP Research In the NewsSeptember marks National Childhood Cancer Awareness Month, and this year at Children’s Hospital of Philadelphia, we kick-started the commemorative period on the heels of exciting news about breakthroughs in pediatric cancer immunotherapy research. Oncology investigators at CHOP also got a big boost in research funding from Hyundai’s nonprofit organization, Hope on Wheels. And that’s only the beginning: Since September marks the return of the football season, we’re thrilled to share the latest headlines on how the National Football League (NFL) is helping to drive concussion research.

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Apr 21 2017

Breastfeeding Practices, Cardiac Life Support, Vaccination Schedules, Face Recognition Diagnosis, American Academy Election, AAPOS Award

CHOP Research In the NewsThis week in the news, those sorts of everyday queries – whether they’re about how to breastfeed, why parents should follow a vaccine schedule, or how mechanical circulatory support devices work – led to exciting headline-making stories.

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Jul 29 2016

CHOP Research In the News: New Rare Disease, FA Woodstock, Bioengineering, and Protecting Toddlers from Child Abuse

CHOP Research In the NewsOne of the things that is so exciting about research at CHOP is that our researchers are working to improve the health and lives of children in such a broad range of ways.

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Dec 29 2015

Research Rewind: A Look Back at 2015

RESEARCHAlthough the year is coming to a close, the research achievements at The Children’s Hospital of Philadelphia in 2015 remain enduring contributions to pediatric health.

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Apr 24 2015

Scientists Explore Gene Silencing as Novel Approach to Dystonia

dystoniaScientists at The Children’s Hospital of Philadelphia are comparing two molecular therapy techniques for Dystonia — RNA interference (RNAi) and antisense oligonucleotides (ASOs).

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Jan 12 2015

Researchers Lay Groundwork for Novel Therapy for Huntington’s Disease

Huntington’s DiseaseResearchers in the Center for Cellular and Molecular Therapeutics (CCMT) at The Children’s Hospital of Philadelphia suggest that an intricate pathway crucial to the development of Huntington’s disease (HD) rests on a “biological teeter-totter” that when carefully balanced could help to control this devastating neurodegenerative disorder.

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Jan 16 2014

Repairing DNA, One Cell at a Time

blindnessHigh is one of the world’s leading experts in gene therapy, which has long been a “next big thing” in medicine: Take a person with a devastating genetic disease and replace their nonfunctional gene with a normal one — a cure built right into your DNA.

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Dec 11 2013

CHOP Hematologist and Gene Therapy Researcher Honored

High, gene thereapy, Children's Hospital, hemophiliaFor her pioneering hemophilia and gene therapy research, Children’s Hospital hematologist Katherine A. High, MD, director of the Center for Cellular and Molecular Therapeutics (CCMT), was recently honored with the 2013 E. Donnall Thomas Lecture and Prize at the American Society of Hematology (ASH) Annual Meeting.

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