Tag Archive: Late Infantile Neuronal Ceroid Lipofuscinosis

Nov 12 2015

Targeted Gene Therapy Aimed at Devastating Childhood Disease

When something important is missing, we often search for a replacement. After many years of looking, a team of researchers at The Children’s Hospital of Philadelphia and the University of Missouri have found a way to substitute for a missing gene linked to a relentless childhood neurodegenerative disease.

Permanent link to this article: http://blog.research.chop.edu/targeted-gene-therapy-aimed-at-devastating-childhood-disease/