Using gene therapy to produce a mutant human protein with unusually high blood-clotting power, scientists have successfully treated animals with the bleeding disorder hemophilia.
Tag Archive: hemophilia
Permanent link to this article: http://blog.research.chop.edu/investigation-bolsters-use-of-variant-protein-in-hemophilia-gene-therapy/
Aug 22 2014
Permanent link to this article: http://blog.research.chop.edu/award-will-support-novel-hemophilia-therapy-investigation/
Dec 11 2013
For her pioneering hemophilia and gene therapy research, Children’s Hospital hematologist Katherine A. High, MD, director of the Center for Cellular and Molecular Therapeutics (CCMT), was recently honored with the 2013 E. Donnall Thomas Lecture and Prize at the American Society of Hematology (ASH) Annual Meeting.
Permanent link to this article: http://blog.research.chop.edu/chop-hematologist-gene-therapy-researcher-honored/