Tag Archive: Canavan disease

Dec 28 2012

Gene Therapy Shows Promise For Helping Children With Canavan Disease

Canavan disease is a rare inherited neurological disorder with devastating effect. The lack of a specific enzyme, called aspartoacylase, causes the body’s central nervous system to break down. The disease is usually fatal before a child reaches the teenage years.

Permanent link to this article: http://blog.research.chop.edu/gene-therapy-shows-promise-for-helping-children-with-canavan-disease/