Category Archive: Hematology

Apr 22 2015

Investigation Bolsters Use of Variant Protein in Hemophilia Gene Therapy

Using gene therapy to produce a mutant human protein with unusually high blood-clotting power, scientists have successfully treated animals with the bleeding disorder hemophilia.

Permanent link to this article: http://blog.research.chop.edu/investigation-bolsters-use-of-variant-protein-in-hemophilia-gene-therapy/

Aug 22 2014

Award Will Support Novel Hemophilia Therapy Investigation

The Children’s Hospital of Philadelphia’s Lacramioara Ivanciu, PhD, was one of five investigators who recently received funding through the Bayer Hemophilia Awards Program (BHAP).

Permanent link to this article: http://blog.research.chop.edu/award-will-support-novel-hemophilia-therapy-investigation/

Jul 23 2014

Platelet Granule Formation Gives Insight Into Rare Disease

Cell biologists at The Children’s Hospital of Philadelphia Research Institute speculate that platelet granules hold the key to unlocking the mechanisms behind Hermansky-Pudlak syndrome.

Permanent link to this article: http://blog.research.chop.edu/platelet-granule-formation-gives-insight-rare-disease/

Aug 06 2013

Reprogramming Stem Cells to Treat, Study Disease

In two new studies, investigators from CHOP reprogrammed skin cells from patients with rare disorders into induced pluripotent stem cells (iPSCs).

Permanent link to this article: http://blog.research.chop.edu/reprogramming-stem-cells-to-treat-study-disease/